Regeneron Strikes A CHORD With Deafness Gene Therapy

 
• By Elizabeth Cairns
  
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A very early success with a gene therapy for a rare form of deafness puts Regeneron ahead of Lilly and Sensorion.  

Ear of child
• Source: Shutterstock

There are no approved pharmacological therapies for congenital hearing loss and this situation is unlikely to change any time soon. Still, a glimmer of hope has been provided with signs of hearing improvement in a single patient with profound genetic deafness after treatment with Regeneron Pharmaceuticals, Inc.’s gene therapy, DB-OTO.

Key Takeaways
  • The first patient treated with Regeneron’s gene therapy for genetic deafness, DB-OTO, has shown signs of hearing improvement

The asset is designed to transfer a functional copy of the gene for otoferlin to patients whose deafness is caused...

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