Value-Based Agreements On The Cards For UniQure/CSL’s $3.5m Hemophilia B Gene Therapy

On Top Of Up To 30% Discounts

While Hemgenix has courted criticism since its $3.5m price tag was unveiled, a drug pricing expert has told Scrip discounts and value-based agreements could make the therapy more palatable to payers.

Animated dollar bills and coins
Value-Based Agreements Help Parse Out Risks Associated With Expensive Therapies • Source: Shutterstock

uniQure N.V./CSL Limited’s hemophilia B gene therapy Hemgenix’s (etranacogene dezaparvovec) $3.5m price tag could be softened through discounts and value-based agreements (VBAs) intended to parse out risk and enhance accessibility.

CSL revealed Hemgenix’s hefty upfront cost after it won US Food and Drug Administration approval for severe hemophilia B on...

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