Sickle Cell Gene Therapy: Medicaid Needs Solutions For High Upfront Costs Soon

 
• By Cathy Kelly
  
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With gene therapies for sickle cell disease looming and two new expensive therapies of to a slow start, access challenges could prevent a large portion of patients from receiving treatment, a report from the US National Academies of Sciences, Engineering and Medicine concludes. The report urges development of new payment models, offering five ideas.

Sickle cell anemia, 3D illustration showing blood vessel with normal and deformated crescent-like red blood cells
Sickle Cell Gene Therapy Will Force New Payment Models

As the leading insurers for most of the sickle cell disease population in the US, the Centers for Medicare and Medicaid Services and state Medicaid agencies should identify approaches to financing the upfront costs for high-cost curative therapies over the next two to three years, according to a new report released by the US National Academies of Sciences, Engineering and Medicine on 10 September.

In light of the recent approval of high-cost therapies and the prospect of even more expensive gene therapies on the...

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